Authors: Sharon Salt, Editor
Find out more about the headlines from the 143rd Annual Meeting of the American Neurological Association (ANA2018; 21–23 October, Atlanta, GA, USA) below, which features top abstracts presented from the conference. Highlights include:
Gene therapy shows early signs of improvement in Parkinson’s disease
Investigators at the University of California San Francisco (CA, USA) and the University of Pittsburgh Medical Center (PA, USA) have reported on an early phase clinical trial of adenovirus-delivered gene therapy for the treatment of Parkinson’s disease that is resistant to standard medical treatment.
The presented study assessed the safety and tolerability, AADC activity and functional outcomes following administration of VY-AADC01, an AAV2 gene therapy encoding AADC.