Researchers have revealed that reducing mutant huntingtin protein in the brain could restore cognitive and psychiatric impairments in mice.
Browsing: antisense therapy
Exploring the use of antisense therapy for neurodegenerative diseases: an interview with Frank Bennett
In this interview, Frank Bennett speaks to us about the work on IONIS-HTTRx in patients with early-stage Huntington’s disease and how this therapy could be applied to treat other neurodegenerative diseases.
A potential new therapeutic for inherited amyotrophic lateral sclerosis, which extended survival and reversed fatal neuromuscular damage in rodents, has entered Phase I/II clinical trials.