PTC Therapeutics (NJ, USA) has announced positive topline results from part II of the FIREFISH trial, demonstrating that risdiplam was well tolerated in infants with Type 1 spinal muscular atrophy.
Browsing: Development and pediatrics
The amount of sleep we get could be associated with certain miRNAs, according to a study investigating miRNA levels in children and adolescents. This could potentially lead to a blood test to reveal sleep deprivation.
New research presented at SfN Neuroscience 2019 outlines some of the exciting developments and important limitations in the use of brain organoids as models for human cortical development.
Three studies presented at SfN Neuroscience 2019 reveal advancements in autism research that could improve intervention and treatment.
By manipulating molecular models, researchers discover protein that could accelerate recovery from peripheral nerve injury.
For the first time in living animals, researchers have tracked the movement and functional activity of neurons as they wired together into circuits and discovered that motor neurons are the first to send signals.
In the largest study of its kind, researchers discovered that testosterone does not impair cognitive empathy, challenging the notion of autism as reflecting an ‘extreme male brain’.
Researchers have developed ’mini-brains’ with optimized cellular network activity, which exhibit similar electrical impulse patterns observed in premature infants.
In this Editorial, published in the journal Future Neurology, the author discusses the need for continued funding for spinal muscular atrophy.
New research suggests that exosomes could play an important role in brain circuits, cell signaling and cell communication.